--- title: Rare Disease CROs path: /indications/rare-disease companies_count: 47 --- # Rare Disease CROs 47 published CROs match Rare Disease. Locations in this set include United States, China, United Kingdom, France, Australia, and India. Capabilities that show up most often in this set: Regulatory Affairs, Clinical Operations, Phase II Clinical Trials, Phase III Clinical Trials, and Phase I Clinical Trials. ## Matching companies - [Accelsiors](/companies/accelsiors) - Full-service CRO providing clinical trial management, regulatory consulting, pharmacovigilance, biostatistics, and medical writing across 40+ countries with AI-secure eClinical systems and patient-centered trial design. - [Aldeyra Therapeutics](/companies/aldeyra) - Biopharmaceutical company developing immunomodulatory therapies for immune-mediated ocular and systemic diseases, with late-stage clinical candidates targeting dry eye disease, allergic conjunctivitis, and retinal conditions. - [Allucent](/companies/allucent) - Allucent is a full-service CRO specializing in clinical development solutions for small and mid-sized biotech companies. - [Aragen Life Sciences](/companies/aragen) - Global CRDMO partner offering integrated discovery-to-commercialization services across small molecules and biologics, with 4000+ scientists and R&D/manufacturing campuses in Asia, North America, and Europe. - [Aroga Biosciences, Inc.](/companies/arogabio) - Full-service CRO providing regulatory writing, medical writing, quality control, regulatory operations, and submission management for biotech and pharmaceutical projects. - [CTI Clinical Trial and Consulting Services](/companies/ctifacts) - Full-service CRO founded in 1999 providing therapeutic expertise across clinical trial and consulting services to pharmaceutical and biotechnology companies. - [Caidya](/companies/caidya) - Caidya is a global, full-service CRO delivering personalized clinical development solutions across all phases of clinical research. - [Cassia, LLC](/companies/cassiallc) - Cassia, LLC is a San Diego-based CRO specializing in green chemo-enzymatic synthesis of stable-isotope labeled metabolites, proteins, and nucleic acids, plus LC-MS/MS RNA modification mapping services for discovery and therapeutic development. - [Certara](/companies/certara) - Certara transforms drug development with proprietary biosimulation software, predictive modeling, and AI-driven services spanning discovery through commercialization. Serving 2,400+ biopharmaceutical companies and regulatory agencies across 70 countries, Certara's model-informed drug development (MIDD) platform accelerates clinical and regulatory decision-making. - [Clarenta](/companies/comac-medical) - Clarenta (formerly Comac Medical Group) is a pan-European CRO offering full-service trial delivery and early-phase studies, including first-in-human and PK work. It runs a Phase I unit in Sofia and has depth in oncology and rare diseases. - [Clario](/companies/clario) - Clario provides comprehensive clinical trial endpoint solutions spanning cardiac safety, eCOA, medical imaging, respiratory, and precision motion analysis, supporting approximately 70% of FDA and EMA novel drug approvals over the past decade. - [Clinilabs](/companies/clinilabs) - Clinilabs is the leading CNS-focused CRO with 25+ years of expertise in neurotherapeutic clinical trials, offering Phase 1–4 trial management, early-phase development, clinical research units, and MedTech device expertise across psychiatry, neurology, substance use, and rare CNS disorders. - [Critical Path Institute](/companies/critical-path-institute) - Critical Path Institute convenes pharmaceutical, government, patient, and academic organizations to optimize drug and medical product development through collaborative consortia, regulatory science initiatives, and clinical trial design optimization. - [Cyagen Biosciences](/companies/apac-cyagen) - Cyagen provides genetically engineered animal models, custom cell lines, and viral packaging services for preclinical research, with specialized expertise in humanized mice, gene therapy vectors, and disease-specific models across oncology, neurology, and metabolic disorders. - [ERGOMED Group](/companies/ergomed) - Global, full-service CRO specializing in oncology and rare disease clinical development, with complementary pharmacovigilance and QA consulting brands. - [Ergomed Clinical Research](/companies/medsource) - Ergomed is a specialized CRO with 25+ years of experience delivering oncology, rare disease, and complex clinical trial solutions across all phases globally, backed by a team of 100+ MDs and PhDs. - [ExperTrials](/companies/expertrials) - European-based full-service CRO supporting biotech and medtech companies from Phase I through Phase IV and market access, with 80+ senior clinical research associates across Europe and the USA. - [Fortrea](/companies/fortrea) - Fortrea is a leading CRO advancing clinical trials through patient-focused clinical solutions that accelerate clinical development and drive trial success. - [GemPharmatech](/companies/gempharmatech) - GemPharmatech develops and supplies genetically engineered mouse models (GEMMs) and preclinical research services using CRISPR/Cas9 and gene-editing technologies, with a library of 25,000+ mouse strains including KO/cKO, humanized, and immunodeficient models. - [ICON plc](/companies/iconplc) - ICON is a global clinical research organization providing full-service drug development and clinical trial solutions across early phase through post-marketing, including clinical operations, bioanalytical labs, cardiac safety, medical imaging, and regulatory affairs.