Rare Disease CROs in United States
25 published
25 published CROs match Rare Disease in United States.
Locations in this set include United States, United Kingdom, China, Australia, France, and India.
Capabilities that show up most often in this set: Regulatory Affairs, Clinical Operations, Phase I Clinical Trials, Phase II Clinical Trials, and Phase III Clinical Trials.
Matching companies
Aragen Life SciencesGlobal CRDMO partner offering integrated discovery-to-commercialization services across small molecules and biologics, with 4000+ scientists and R&D/manufacturing campuses in Asia, North America, and Europe.
Aroga Biosciences, Inc.Full-service CRO providing regulatory writing, medical writing, quality control, regulatory operations, and submission management for biotech and pharmaceutical projects.
CTI Clinical Trial and Consulting ServicesFull-service CRO founded in 1999 providing therapeutic expertise across clinical trial and consulting services to pharmaceutical and biotechnology companies.
Cassia, LLCCassia, LLC is a San Diego-based CRO specializing in green chemo-enzymatic synthesis of stable-isotope labeled metabolites, proteins, and nucleic acids, plus LC-MS/MS RNA modification mapping services for discovery and therapeutic development.
CertaraCertara transforms drug development with proprietary biosimulation software, predictive modeling, and AI-driven services spanning discovery through commercialization. Serving 2,400+ biopharmaceutical companies and regulatory agencies across 70 countries, Certara's model-informed drug development (MIDD) platform accelerates clinical and regulatory decision-making.
ClarentaClarenta (formerly Comac Medical Group) is a pan-European CRO offering full-service trial delivery and early-phase studies, including first-in-human and PK work. It runs a Phase I unit in Sofia and has depth in oncology and rare diseases.
ClinilabsClinilabs is the leading CNS-focused CRO with 25+ years of expertise in neurotherapeutic clinical trials, offering Phase 1–4 trial management, early-phase development, clinical research units, and MedTech device expertise across psychiatry, neurology, substance use, and rare CNS disorders.
Cyagen BiosciencesCyagen provides genetically engineered animal models, custom cell lines, and viral packaging services for preclinical research, with specialized expertise in humanized mice, gene therapy vectors, and disease-specific models across oncology, neurology, and metabolic disorders.
ERGOMED GroupGlobal, full-service CRO specializing in oncology and rare disease clinical development, with complementary pharmacovigilance and QA consulting brands.- Ergomed Clinical ResearchErgomed is a specialized CRO with 25+ years of experience delivering oncology, rare disease, and complex clinical trial solutions across all phases globally, backed by a team of 100+ MDs and PhDs.
ExperTrialsEuropean-based full-service CRO supporting biotech and medtech companies from Phase I through Phase IV and market access, with 80+ senior clinical research associates across Europe and the USA.
FortreaFortrea is a leading CRO advancing clinical trials through patient-focused clinical solutions that accelerate clinical development and drive trial success.
ICON plcICON is a global clinical research organization providing full-service drug development and clinical trial solutions across early phase through post-marketing, including clinical operations, bioanalytical labs, cardiac safety, medical imaging, and regulatory affairs.
KCAS BioLeading bioanalytical CRO with 45+ years of experience, supporting 315+ approved drugs through bioanalysis, biomarker, immunogenicity, flow cytometry, and clinical kitting services across US, EU, and Australia facilities.
MedpaceFull-service CRO with 30+ years of organic growth, offering integrated clinical development services across all phases with wholly-owned central labs, bioanalytical lab, imaging core lab, and Phase I unit.
NorthernBioMichigan-based preclinical CRO specializing in targeted drug delivery, molecular biology, and bioanalysis with three GLP-compliant facilities supporting non-GLP and GLP safety assessment studies.
PPDPPD is a leading global contract research organization (CRO) and the clinical research business of Thermo Fisher Scientific.
PerceptiveLeading clinical research organization providing preclinical to late-phase imaging, randomization and trial supply management (RTSM), and eClinical services to the global biopharmaceutical industry.
PharmaronPremier life science CRO and CDMO offering integrated R&D and manufacturing across drug discovery, preclinical, clinical development, and commercialization for small molecules, biologics, and cell & gene therapies. 25,000+ employees across China, US, and UK.
Premier ResearchPremier Research is a global full-service CRO delivering clinical research and development solutions across the complete drug development lifecycle. The organization provides comprehensive capabilities spanning study design, study startup, medical affairs, biostatistics and data management, central monitoring, clinical monitoring and site management, project and risk management, safety and pharmacovigilance, quality and compliance, and medical writing.
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